Pre-IND Feasibility Assessment · V0.1 MVP

Enrollment Risk
Intelligence Engine

Clinical Trial Planning Tool · Zonra Inc.
01
Programme
02
Geography
03
Site Profile
04
Constraints
05
Risk Index
Layer 01 — Patient Pool Intelligence
Tell us about your programme
Gene Therapy — Ultra-Rare
fewer than 1:50,000 patients
Gene Therapy — Rare Disease
1:2,000 – 1:50,000 patients
Rare Genetic Disease
monogenic or chromosomal
Rare Metabolic / Enzyme
LSDs, metabolic disorders
Rare Neurological
CNS, neuromuscular
Other Rare Disease
haematology, immunology, other
Pre-IND
discovery to IND filing
IND-Ready
IND filed or imminent
Phase 1 / 1-2
first-in-human planned
Phase 2
dose expansion
Phase 2/3 Pivotal
registration-enabling
Pre-CRO Selection
evaluating CRO partners
Layer 01–02 — Geography & Site Scope
Where will the trial run?
United States Only
FDA-regulated sites
US + Europe
FDA + EMA sites
Global (Standard)
US, EU, Asia-Pacific
Global + AfricaExtended
includes African site mapping
Africa-FocusedExtended
Nigeria and sub-Saharan Africa
Emerging Markets
LATAM, MENA, SE Asia
FDORA Diversity Action Plan Required
FDA mandate for diverse enrollment · race/ethnicity targets required
Layer 02 — Site Capability Assessment
Site & therapy requirements
AAV Gene Therapy
adeno-associated viral vector
Lentiviral / Ex Vivo
cell-based gene therapy
mRNA / ASO / RNA
nucleic acid therapy
Small Molecule / Enzyme
ERT, substrate reduction
Cell Therapy / CAR-T
autologous or allogeneic
Other / Undecided
multiple or TBD
LTFU Monitoring Required (≥ 5 years)
standard for gene therapy — major site capability constraint
Layer 03 — Competitive Landscape & Constraints
Known constraints & competitive context
Active or Planned Competing Trials Known
other sponsors targeting the same patient pool
Patient Registry or Natural History Study Exists
formal registry or NHS / other cohort data available
Urgent
FPI target < 12 months
Moderate
12–24 months to FPI
Flexible
> 24 months to FPI
Layer 04 — Enrollment Risk Index
Your enrollment risk profile
This Enrollment Risk Index is a directional pre-assessment generated by Zonra's feasibility framework. Scores are based on programme parameters and known epidemiological and site capability factors. A full Zonra engagement includes comprehensive patient pool modelling, global site database analysis, competitive landscape mapping, and a live readout with your team — delivered within 3–4 weeks. Zonra Inc. · Delaware, USA · zonra.bio · mariam@zonra.bio